The FDA Is Blocking Treatment for Children with Special Needs. Here’s How | Hannah Cox

Some idiot came up to a friend of mine who has a child with Down's syndrome and asked "why is that child here?"
My question is "who made you God"?

Lt Col Charlie Brown Yes, God doesn't make any "junk".

MSgt Dale Johnson - Agreed. If you were to put the federal government in charge of managing the Sahara Desert, within five years there would be a shortage of sand and widespread flooding.

This is an article about gene therapy (technically, the correct name of the application is "human gene transfer"). I spent 22+ years in my civilian career working in the field. ONLY 2 gene therapy treatments are approved as "standard of care treatment" at this time: on for use in a specific eye disease/ disorder, and gene therapy for spinal muscular atrophy (SMA) which is actually a treatment for use in infants & young children, which the author seems to overlook. ALL others experimental at this time. We have an FDA and review of drugs and treatments because there were actual "snake oil" salesmen pushing adulterated or non functional or toxic materials as drugs and cures. If the government did not perform this service then we'd be back to snake oil sales and buyer beware. There have long been "compassionate use" protocols to request an experimental drug and we do have 'right to try' which is really a right to ask (same as compassionate use) but the private company (pharma) is under no obligation to provide the drug.